Profile of mecasermin for the long-term treatment of growth failure in children and adolescents with severe primary IGF-1 deficiency, Ther Clin Risk Manag, vol.5, pp.553-559, 2009. ,
A Plant-Derived Recombinant Human Glucocerebrosidase Enzyme???A Preclinical and Phase I Investigation, PLoS ONE, vol.321, issue.320, p.4792, 2009. ,
DOI : 10.1371/journal.pone.0004792.s002
Anti-CD20 Antibody Therapy for B-Cell Lymphomas, New England Journal of Medicine, vol.366, issue.21, pp.2008-2016, 2012. ,
DOI : 10.1056/NEJMct1114348
Synthetic protein transduction domains: enhanced transduction potential in vitro and in vivo, Cancer Res, vol.61, pp.474-477, 2001. ,
Cell-penetrating peptides???A brief introduction, Biochimica et Biophysica Acta (BBA) - Biomembranes, vol.1758, issue.3, pp.260-263, 2006. ,
DOI : 10.1016/j.bbamem.2006.02.012
Intracellular Delivery of Proteins with a New Lipid-mediated Delivery System, Journal of Biological Chemistry, vol.19, issue.37, pp.35103-35110, 2001. ,
DOI : 10.1006/bbrc.1995.2838
Intracytoplasmic delivery of anionic proteins, Molecular Therapy, vol.9, issue.6, pp.964-969, 2004. ,
DOI : 10.1016/j.ymthe.2004.03.007
Serum insensitive, intranuclear protein delivery by the multipurpose cationic lipid Saint-2, Journal of Controlled Release, vol.123, issue.3, pp.228-238, 2007. ,
DOI : 10.1016/j.jconrel.2007.08.014
Ligand-targeted liposome design: challenges and fundamental considerations, Trends in Biotechnology, vol.32, issue.1, pp.32-45, 2014. ,
DOI : 10.1016/j.tibtech.2013.09.007
Probing the in vitro mechanism of action of cationic lipid/DNA lipoplexes at a nanometric scale, Nucleic Acids Research, vol.2, issue.4, pp.1595-1609, 2011. ,
DOI : 10.2174/1567201052772889
URL : https://hal.archives-ouvertes.fr/hal-00566862
Cationic lipids, lipoplexes and intracellular delivery of genes, Journal of Controlled Release, vol.116, issue.2, pp.255-264, 2006. ,
DOI : 10.1016/j.jconrel.2006.06.024
Physicochemical Parameters of Non-Viral Vectors that Govern Transfection Efficiency, Current Gene Therapy, vol.8, issue.5, pp.313-323, 2008. ,
DOI : 10.2174/156652308786070961
A frame-shift mutation in the cystic fibrosis gene, Nature, vol.344, issue.6267, pp.665-667, 1990. ,
DOI : 10.1038/344665a0
Processing of mutant cystic fibrosis transmembrane conductance regulator is temperature-sensitive, Nature, vol.358, issue.6389, pp.761-764, 1992. ,
DOI : 10.1038/358761a0
Disruption of cytokeratin-8 interaction with F508del-CFTR corrects its functional defect, Human Molecular Genetics, vol.65, issue.3, pp.623-634, 2012. ,
DOI : 10.1136/thx.2009.123422
Rescue of ??F508-CFTR (Cystic Fibrosis Transmembrane Conductance Regulator) by Curcumin: Involvement of the Keratin 18 Network, Journal of Pharmacology and Experimental Therapeutics, vol.317, issue.2, pp.500-505, 2006. ,
DOI : 10.1124/jpet.105.097667
, , 1996.
, Guanidinium-cholesterol cationic lipids: efficient vectors for the transfection of eukaryotic cells, Proc Natl Acad Sci, vol.93, pp.9682-9686
Paromomycin and neomycin B derived cationic lipids: Synthesis and transfection studies, Journal of Controlled Release, vol.158, issue.3, pp.461-469, 2012. ,
DOI : 10.1016/j.jconrel.2011.12.019
Self-assembled lamellar complexes of siRNA with lipidic aminoglycoside derivatives promote efficient siRNA delivery and interference, Proceedings of the National Academy of Sciences, vol.25, issue.4, pp.16534-16539, 2007. ,
DOI : 10.1006/meth.2001.1262
On the Mechanism of Cationic Amphiphile-mediated Transfection. To Fuse or not to Fuse: Is that the Question?, Journal of Membrane Biology, vol.189, issue.3, pp.167-179, 2002. ,
DOI : 10.1007/s00232-002-1015-7
Novel neutral imidazole-lipophosphoramides for transfection assays, Chemical Communications, vol.278, issue.27, pp.3124-3126, 2008. ,
DOI : 10.1039/b805226c
Gene transfer by chemical vectors, and endocytosis routes of polyplexes, lipoplexes and lipopolyplexes in a myoblast cell line, Biomaterials, vol.33, issue.10, pp.2980-2990, 2012. ,
DOI : 10.1016/j.biomaterials.2011.12.027
URL : https://hal.archives-ouvertes.fr/hal-00721795
Chemical vectors for gene delivery: a current review on polymers, peptides and lipids containing histidine or imidazole as nucleic acids carriers, British Journal of Pharmacology, vol.3, issue.2, pp.166-178, 2009. ,
DOI : 10.1111/j.1476-5381.2009.00288.x
URL : https://hal.archives-ouvertes.fr/hal-00525108
, Biochemistry, vol.35, issue.18, pp.5616-5623, 1996.
DOI : 10.1021/bi9602019
Structural characteristics of supramolecular assemblies formed by guanidinium-cholesterol reagents for gene transfection, Proceedings of the National Academy of Sciences, vol.35, issue.18, pp.2621-2626, 1999. ,
DOI : 10.1021/bi9602019
Design and development of polymers for gene delivery, Nature Reviews Drug Discovery, vol.278, issue.7, pp.581-593, 2005. ,
DOI : 10.1074/jbc.M308643200
Global proteomic approach unmasks involvement of keratins 8 and 18 in the delivery of cystic fibrosis transmembrane conductance regulator (CFTR)/?F508-CFTR to the plasma membrane, PROTEOMICS, vol.103, issue.12, pp.3833-3844, 2004. ,
DOI : 10.1042/cs1030417
Negatively charged self-assembling DNA/poloxamine nanospheres for in vivo gene transfer, Nucleic Acids Research, vol.32, issue.20, p.159, 2004. ,
DOI : 10.1093/nar/gnh153