Functional outcomes FGR Antisense oligonucleotides Maternal behavior Neuromuscular disease Brain injury Biological marker Intra-uterine growth restriction Brain imaging ASOs Coagulation factor IX Brain Effector T cells Cell reprogramming Cellules souches musculaires Genetics Mouse model Maladie neuromusculaire Calcium handling Bone development Aav10 Cartilage and bone regeneration Les paramètres respiratoires AAV Spinal muscular atrophy Gene transfer Long-term handicap Fabry disease lysosomal storage disorders adeno asociated virus-9 Cell stemness Clinical trials GABA Bone involvement MRNP assembly Adenosine Amyotrophie spinale ASO IPSCs Disease modifiers Prematurity Icv LMNA Disease heterogeneity Adult patients Cofilin-1 FTD Amyotrophic Lateral Sclerosis Albumin gene targeting MRI CNS Biomarker Bioinformatics GeneRide MiRNA Genetical therapy Mecp2 C9orf72 Distal myopathy 3xTgAD Mice DPRs Extremely preterm infants CRISPR/SaCas9 Diseases Brain development Errance diagnotique MND Clinical trial Intra-CSF delivery IUGR Melatonin Epigenetic changes Chondrocytes Biomarkers DTI Lentiviral vectors ALS MUNIX Skeletal muscle Longitudinal progression Dicer Fetal growth restriction AICD SMN Gene therapy Adult SMA Microglia Brain MRI IRM G-Secretase Maternal malnutrition ERK1/2 signaling Early-onset sepsis Glucocorticosteroid Dilated cardiomyopathy Clinical markers FOXO3a Brain damage Inflammation Modèle murin Blood brain barrier Duchenne Muscular Dystrophy