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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Ex-vivo
Hepatocellular carcinoma
Animal/physiopathology
Muscles/physiopathology
DMO
Dystrophy
Muscular Dystrophy
Myotendinous junction
MES
Centronuclear myopathy
LKB1
Human Umbilical Vein Endothelial Cells
Genomic
L-Type
Base Sequence
Duchenne muscular dystrophy
Autophagy
Long QT
Cells
Metabolism
Modificateurs de gènes
Dystrophie Musculaire de Duchenne DMD
Cachexia
Gene Expression Regulation/drug effects
Inhibitors
BMD
CD38
Cell Biology
Dystrophin
Drp1
Antisense oligonucleotides
Morphogenesis
NNOS
Exon skipping
Delivery
Muscle
Cell homeostasis
Muscular dystrophy
Muscular Atrophy
Cultured
Muscle Strength
Myogenesis
Dynamin 2
Dystrophine
Activin Receptors
Mitochondrial fission
Duchenne muscular dystrophy DMD
Calcium
Invivo
Dystrophie Musculaire de Becker BMD
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
LncARN
Génomique
Dystrophie musculaire de Becker
Gene modifiers
Allele‐specific silencing therapy
Knockout
Muscle Biology
Becker muscular dystrophy BMD
Duchenne DMD dystrophy
Inbred mdx
Male
Multiresolution modeling
Molecular Sequence Data
Multi resolution modeling
NAD+
Clinical trials
MiARN
Cardiomyopathy
Muscle development
Becker BMD muscular dystrophy
Dystrophin central domain
Molecular docking
Cell Line
DHPR α1S
Energy Metabolism/drug effects
Dystrophin-EGFP
DMD
CaV subunits
Humans
Multi exon skipping
Liver
Homeostasis
Long noncoding RNA
Animals
Epigenetics
LncRNA
Inbred C57BL
CaVβs
Mice
Cardiomyopathie
Becker muscular dystrophy
Immunoglobulin Fc Fragments/pharmacology
Diseases
Hear
Calcium Channels
Skeletal muscle
CTNNB1
Mdx mouse
Gene expression